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|NCT01873911 : Neurobehavioral Phenotypes in MPS III|
|Ages||Min: 2 Years Max: 12 Years|
Research Subjects: Verified diagnosis of MPS IIIA or MPS IIIB (having proof of either
genetic mutation or enzymatic analysis prior to enrollment in this study); must be between
the ages of 2 and 12 years; must be able to walk.
Control group: Verified diagnosis of MPS IH; must have already undergone hematopoietic
cell transplantation in the past; must be aged between 2 and 5 years; and must be able to
walk without support.
Participants will be excluded who are unable to cooperate or comply with this study's
procedures; in the opinion of the principal investigator, participants who have other
severely-limiting co-existing conditions such as severe hearing or visual impairment, will
be excluded from this study.
|Links||Permanent Link to THIS page: https://virtualtrials.com/nct/display1trial.cfm?nct=NCT01873911
| Link to official Clinicaltrials.gov listing